The Pinball Lounge at 78th Street Sudios offers an ideal setting for this unique fundraiser. The event runs from 4-6 pm, providing families with an accessible Sunday afternoon activity. True to its ...

Angelman syndrome is a rare genetic disorder that impacts brain development, speech, movement, and learning.

Colin Farrell has opened up on his difficult decision to place his disabled son in long-term care. James was born to Colin and ex-partner US model Kim Bordenave. The youngster was diagnosed with the ...

ORLANDO, Fla.--(BUSINESS WIRE)--Encoded Therapeutics Inc., a clinical-stage biotechnology company developing genetic medicines for severe central nervous system (CNS) disorders, announced today that ...

NOVATO, Calif., Feb. 05, 2024 (GLOBE NEWSWIRE) -- Ultragenyx Pharmaceutical Inc. (RARE) today announced that the European Medicines Agency (EMA) has granted Priority Medicine (PRIME) designation to ...